A Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in Late-infantile and Juvenile Forms of Niemann-Pick Type C Disease, GM1 Gangliosidosis or GM2 Gangliosidosis
PHASE3
An 18-month double-blind, randomized, placebo-controlled, multicenter, Phas...
Status
Recruiting
Location
UCSF Children's Hospital and Research Center at Oakland
Olaparib in Treating Patients With Relapsed or Refractory Advanced Solid Tumors, Non-Hodgkin Lymphoma, or Histiocytic Disorders With Defects in DNA Damage Repair Genes (A Pediatric MATCH Treatment Trial)
PHASE2
This phase II Pediatric MATCH trial studies how well olaparib works in trea...
Samotolisib in Treating Patients With Relapsed or Refractory Advanced Solid Tumors, Non-Hodgkin Lymphoma, or Histiocytic Disorders With TSC or PI3K/MTOR Mutations (A Pediatric MATCH Treatment Trial)
PHASE2
This phase II Pediatric MATCH trial studies how well samotolisib works in t...